Development Plan FDA and EMA Approval

The advent of effective enzyme therapies for the visceral manifestations of Gaucher disease has stimulated renewed interest in both the basic science and therapeutics for the neuronopathic Gaucher disease variants, types 2 and 3.  In numerous Scientific  workshops, led by Dr. Tony Futerman and hosted by the PBRF, basic scientists discussed the mechanisms causing the brain disease in Gaucher disease.  The discussion was vigorous and will lead to many interesting and important discoveries related to the neurologic involvement in Gaucher disease. Continue reading Development Plan FDA and EMA Approval

Award “Best in America Seal” of excellence

Each year the Parkinson’s & Brain Research Foundation provides a Financial Audit and endures a rigorous approval process for acceptance into US Federal Government  fundraising campaigns. Through this process  we have earned exclusive recognition with the award of the “Best In America Seal”. Below is the description of this honor as represented by the Independent Charities of America:

“The Independent Charities Seal of Excellence is awarded to the members of Independent Charities of America and Local Independent Charities of America that have, upon rigorous independent review, been able to certify, document, and demonstrate on an annual basis that they meet the highest standards of public accountability, program effectiveness, and cost effectiveness.  These standards include those required by the US Government for inclusion in the Combined Federal Campaign, probably the most exclusive fund drive in the world.  Of the 1,000,000 charities operating in the United States today, it is estimated that fewer than 50,000, or 5 percent, meet or exceed these standards, and, of those, fewer than 2,000 have been awarded this Seal.”

Remember: 98% of your donation goes to medical research.